- The Cure from CRISPR Classroom
- First Drug Ever for Friedrich’s Ataxia Approved
First Drug Ever for Friedrich’s Ataxia Approved
Plus: Promising New Treatment for Hidradenitis Suppurativa
Hi friends 👋🏼,
I finally got a PS5 and dived right into playing the latest Star Wars game! As I zipped through those awesome galaxies, it hit me how puzzling and intricate the game is - kind of like clinical trials. So, I hit the pause button on gaming and wrote Clinical Trials 101 to help you unravel the twists and turns of clinical trials without the jargon.
How’d you like my transition from Star Wars to clinical trials. Corny, I’m sure 😂
Either way, we’ve got a brand new approval for you this week, plus more cool science:
First Drug Ever for Friedreich’s Ataxia Approved READER REQUEST
Promising New Treatment for Hidradenitis Suppurativa READER REQUEST
New Clinical Data for Sickle Cell CRISPR Therapy READER REQUEST
Combating Polycythemia Vera READER REQUEST
🎊 First Drug for Friedreich’s Ataxia Approved
Patient with severe skeletal deformations as a result of FA
Friedreich’s ataxia (FA) is a debilitating neurological disease that progressively damages the brain, nervous system, and muscles, leading to severe impairments. Until now, there were no approved treatments, and severe patients had a life expectancy in the mid-30s.
February, 2023 marked a historic month for the patient community as the first drug to fight FA was approved! 👇🏼
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